dc.contributorUniv Cambridge
dc.contributorHosp Ninos Dr Ricardo Gutierrez
dc.contributorHEMORIO
dc.contributorMt Sinai Hosp
dc.contributorCincinnati Childrens Hosp Med Ctr
dc.contributorUniversidade Federal de São Paulo (UNIFESP)
dc.contributorMinist Publ Hlth Russia
dc.contributorCedars Sinai Tower Hematol Oncol
dc.contributorGenzyme
dc.creatorCox, Timothy M.
dc.creatorDrelichman, Guillermo
dc.creatorCravo, Renata
dc.creatorBalwani, Manisha
dc.creatorBurrow, Thomas Andrew
dc.creatorMartins, Ana Maria [UNIFESP]
dc.creatorLukina, Elena
dc.creatorRosenbloom, Barry
dc.creatorRoss, Leorah
dc.creatorAngell, Jennifer
dc.creatorPuga, Ana Cristina
dc.date.accessioned2016-01-24T14:35:15Z
dc.date.available2016-01-24T14:35:15Z
dc.date.created2016-01-24T14:35:15Z
dc.date.issued2014-02-01
dc.identifierMolecular Genetics and Metabolism. San Diego: Academic Press Inc Elsevier Science, v. 111, n. 2, p. S33-S33, 2014.
dc.identifier1096-7192
dc.identifierhttp://repositorio.unifesp.br/handle/11600/37397
dc.identifier10.1016/j.ymgme.2013.12.061
dc.identifierWOS:000330746000051
dc.languageeng
dc.publisherElsevier B.V.
dc.relationMolecular Genetics and Metabolism
dc.rightshttp://www.elsevier.com/about/open-access/open-access-policies/article-posting-policy
dc.rightsAcesso restrito
dc.titleENCORE: A randomized, controlled, open-label non-inferiority study comparing eliglustat to imiglucerase in Gaucher disease type 1 patients on enzyme replacement therapy who have reached therapeutic goals
dc.typeResumo


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