Resumo
ENCORE: A randomized, controlled, open-label non-inferiority study comparing eliglustat to imiglucerase in Gaucher disease type 1 patients on enzyme replacement therapy who have reached therapeutic goals
Fecha
2014-02-01Registro en:
Molecular Genetics and Metabolism. San Diego: Academic Press Inc Elsevier Science, v. 111, n. 2, p. S33-S33, 2014.
1096-7192
10.1016/j.ymgme.2013.12.061
WOS:000330746000051
Autor
Cox, Timothy M.
Drelichman, Guillermo
Cravo, Renata
Balwani, Manisha
Burrow, Thomas Andrew
Martins, Ana Maria [UNIFESP]
Lukina, Elena
Rosenbloom, Barry
Ross, Leorah
Angell, Jennifer
Puga, Ana Cristina